Substance / Medication

Atidarsagene autotemcel

Overview

Active Ingredient
atidarsagene autotemcel
RxNorm CUI
2677916

Indications & Related Conditions

Conditions associated via SNOMED clinical relationships

Administration & Protocol

Dosing, route, and treatment protocol

Administration details including route, dosing schedules, preparation instructions, and contraindications are pending physician authorship.

Monitoring & Follow-Up

Biomarkers relevant to this intervention via related conditions

No monitoring biomarkers have been mapped yet. Biomarker-intervention linkages are derived through related conditions and will expand as the knowledge graph grows.

Research Evidence

Published studies and systematic reviews

Sort:
Atidarsagene autotemcel for metachromatic leukodystrophy.
Messina Martina, Gissen Paul · Drugs Today (Barc) · 2023
PMID: 36811406Review
Effects of atidarsagene autotemcel gene therapy on peripheral nerves in late-infantile metachromatic leukodystrophy.
Zambon Alberto A, Rancoita Paola M V, Quattrini Angelo et al. · Brain · 2025
PMID: 40286327Other
Atidarsagene autotemcel for metachromatic leukodystrophy.
Fahim Shahariar Mohammed, Lin Grace, Suh Kangho et al. · J Manag Care Spec Pharm · 2024
PMID: 38308621OtherFull text (PMC)
Long-Term Effects of Atidarsagene Autotemcel for Metachromatic Leukodystrophy.
Fumagalli Francesca, Calbi Valeria, Gallo Vera et al. · N Engl J Med · 2025
PMID: 40267426Trial

Research data from MEDLINE/PubMed

Benefits & Expected Outcomes

Benefits, expected outcomes, efficacy data, and NNT (Number Needed to Treat) are pending physician authorship and evidence review.

Risks & Side Effects

Risk profile, common and serious adverse effects, contraindications, and drug interactions are pending physician authorship.

Related Symptoms

Symptoms associated with conditions this intervention addresses

No related symptoms have been mapped yet. Symptom linkages are derived through associated conditions.

Alternatives & Comparisons

Alternative treatments, comparison data, and clinical decision support are pending physician authorship.

Medical Disclaimer

This information is for educational purposes only and does not constitute medical advice, diagnosis, or treatment. Always consult with a qualified healthcare provider regarding any medical condition or treatment plan.

Do not start, stop, or change any treatment without consulting your healthcare provider.

Quick Facts

Type
Substance / Medication
Fully Specified Name
Atidarsagene autotemcel (substance)
SNOMED CT
1363393003
UMLS CUI
C5556517
RxNorm CUI
2677916

Clinical Data

This intervention maps to 1 entities in the Ltrl knowledge graph.

1
Conditions
0
Biomarkers
0
Specialists
0
Symptoms

Data is sourced from SNOMED CT, UMLS, and the Ltrl clinical knowledge graph. Content sections marked as pending require physician authorship. Consult a healthcare provider before starting any treatment.