Substance / Medication

Taliglucerase alfa

Overview

Active Ingredient
taliglucerase alfa
RxNorm CUI
1291609

Indications

ELELYSO is indicated for the treatment of patients 4 years of age and older with a confirmed diagnosis of Type 1 Gaucher disease.

Labeler: Pfizer Laboratories Div Pfizer IncUpdated: 2025-12-29T00:00:00.000ZFull label on DailyMed

Boxed Warning

FDA Black Box Warning

Patients treated with enzyme replacement therapies have experienced life‑threatening hypersensitivity reactions, including anaphylaxis. Anaphylaxis has occurred during the early course of enzyme replacement therapy and after extended duration of therapy. [see Initiate ELELYSO in a healthcare setting

Contraindications

When this intervention should not be used

None.

Indications & Related Conditions

Conditions associated via SNOMED clinical relationships

Administration & Protocol

Dosing, route, and treatment protocol

Detailed dosage and administration information is available in the full FDA drug label.

View full prescribing information on DailyMed

Monitoring & Follow-Up

Biomarkers relevant to this intervention via related conditions

No monitoring biomarkers have been mapped yet. Biomarker-intervention linkages are derived through related conditions and will expand as the knowledge graph grows.

Clinical Trials

2 trials linked to this intervention

2
Total Trials
0
Recruiting
2
With Results

Research Evidence

Published studies and systematic reviews

Sort:
Taliglucerase alfa in Gaucher disease: Description of a Brazilian experience.
Cravo R, Rotman V, Oliveira P M N et al. · Blood Cells Mol Dis · 2018
PMID: 28131618Observational
Safety and efficacy of two dose levels of taliglucerase alfa in pediatric patients with Gaucher disease.
Zimran Ari, Gonzalez-Rodriguez Derlis Emilio, Abrahamov Aya et al. · Blood Cells Mol Dis · 2015
PMID: 25453586Observational
Pharmacokinetics of Novel Plant Cell-Expressed Taliglucerase Alfa in Adult and Pediatric Patients with Gaucher Disease.
Abbas Richat, Park Glen, Damle Bharat et al. · PLoS One · 2015
PMID: 26053270ObservationalFull text (PMC)
Ten-Year Follow-Up of Taliglucerase Alfa in Type 1 Gaucher Disease: Real-World Evidence from Albania.
Cullufi Paskal, Velmishi Virtut, Troja Erjon et al. · J Clin Med · 2025
PMID: 41096096OtherFull text (PMC)
Taliglucerase alfa in the longterm treatment of children and adolescents with type 1 Gaucher disease: the Albanian experience.
Cullufi Paskal, Tomori Sonila, Velmishi Virtut et al. · Front Pediatr · 2024
PMID: 38464899OtherFull text (PMC)
Skeletal Manifestations, Bone Pain, and BMD Changes in Albanian Type 1 Gaucher Patients Treated with Taliglucerase Alfa.
Velmishi Virtut, Troja Erjon, Tanka Marjeta et al. · J Osteoporos · 2023
PMID: 38090017OtherFull text (PMC)
Real-World Experiences with Taliglucerase Alfa Home Infusions for Patients with Gaucher Disease: A Global Cohort Study.
Revel-Vilk Shoshana, Mansfield Royston, Feder-Krengel Neta et al. · J Clin Med · 2023
PMID: 37762854OtherFull text (PMC)
Open-label, expanded access study of taliglucerase alfa in patients with Gaucher disease requiring enzyme replacement therapy.
Kuter David J, Wajnrajch Michael, Hernandez Betina et al. · Blood Cells Mol Dis · 2020
PMID: 32146279Trial

Research data from MEDLINE/PubMed

Benefits & Expected Outcomes

Benefits, expected outcomes, efficacy data, and NNT (Number Needed to Treat) are pending physician authorship and evidence review.

Risks & Side Effects

Adverse reaction and safety data for this drug is sourced from the FDA-approved label.

View adverse reactions & drug interactions on DailyMed

Related Symptoms

Symptoms associated with conditions this intervention addresses

No related symptoms have been mapped yet. Symptom linkages are derived through associated conditions.

Alternatives & Comparisons

Alternative treatments, comparison data, and clinical decision support are pending physician authorship.

Medical Disclaimer

This information is for educational purposes only and does not constitute medical advice, diagnosis, or treatment. Always consult with a qualified healthcare provider regarding any medical condition or treatment plan.

Do not start, stop, or change any treatment without consulting your healthcare provider.

Quick Facts

Type
Substance / Medication
Fully Specified Name
Taliglucerase alfa (substance)
SNOMED CT
708713007
UMLS CUI
C3273401
RxNorm CUI
1291609
Labeler
Pfizer Laboratories Div Pfizer Inc

Clinical Data

This intervention maps to 3 entities in the Ltrl knowledge graph.

3
Conditions
0
Biomarkers
0
Specialists
0
Symptoms
2
Clinical Trials

Data is sourced from SNOMED CT, UMLS, and the Ltrl clinical knowledge graph. Content sections marked as pending require physician authorship. Consult a healthcare provider before starting any treatment.